Inaugural 'Benefit for the Brain'
June 03, 2017
We are hosting our inaugural 'Benefit for the Brain' in Tulsa, OK on July 12th at 7 pm. We hope to see you there!
Gene Therapy Shows Promise for Patients
January 17, 2017
A clinical trial is helping two children from Philadelphia with MLD.
New Cell Therapy Research Into Remyelination
August 18, 2016
An investigative cell therapy product shows promise in accelerating brain remyelination in mice studies.
Exome Sequencing Aids in Leukodystrophy Diagnoses
May 09, 2016
A combination of standard diagnostic imaging tests and exome sequencing significantly boosts the chances for accurate diagnoses.
Screening Tests Could Improve Diagnosis of Two Rare Childhood Diseases
January 05, 2016
Newborn screenings for metachromatic leukodystrophy could greatly benefit patients.